Researchers at MIT have developed a new AI method to design nanoparticles that can deliver RNA vaccines and other RNA-based treatments more effectiv ...

Wall Street analysts boosted their targets on Ionis Pharmaceuticals after the FDA approved its RNA-based drug Dawnzera for ...

In June, the monoclonal antibody garadacimab (Andembry) was approved for prevention of HAE attacks at a dose of once monthly ...

Single-cell proteomics with RNA sequencing uncover hidden gene expression dynamics in stem cell differentiation.

Sarepta is facing a number of issues currently, including platform-level safety concerns, management credibility issues, etc.

In the past decade there has been significant interest in studying the expression of our genetic code down to the level of ...

An announcement from Ionis Pharmaceuticals ( (IONS) ) is now available. On August 21, 2025, Ionis Pharmaceuticals announced that the FDA approved DAWNZERA™ (donidalorsen) for preventing hereditary ...

The approval makes donidalorsen the only treatment in the US for hereditary angioedema that is an RNA-targeted prophylactic.

The ability to correct disease-causing genetic mistakes using genome editors holds great promise in medicine, but it is not ...

Senior author Elias Sayour, M.D., Ph.D., a UF Health pediatric oncologist, said the results reveal a potential new treatment path — an alternative to surgery, radiation, and chemotherapy — with broad ...

A previously unknown virus in farmed Pacific oysters may hold the key to mass die-offs in the multimillion-dollar industry, according to research from the University of British Columbia (UBC) in ...

The quest for a vaccine against HIV has been going on for about 40 years — almost as long as the virus that causes AIDS has ...