A father will soon take on a half marathon following his five-year-old son’s diagnosis with a muscle-wasting condition, which ...

John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the latest ...

The antimalarial drug mefloquine could help treat genetic diseases such as cystic fibrosis, Duchenne muscular dystrophy, as ...

Multidisciplinary coordination across prescribing teams, nursing, laboratory medicine, finance, and infusion centers is crucial for gene therapy delivery in Duchenne muscular dystrophy (DMD).

John Brandsema, MD, a pediatric neurologist at Children’s Hospital of Philadelphia, speaks with Healio about the current understanding of the genetic factors behind muscular dystrophy.

Duchenne muscular dystrophy (DMD) patients in Scotland have not been able to get the drug – which is available in England – despite manufacturers offering it to health boards for free on an ...

Just a few weeks after Avidity Biosciences made a stir with new data on its experimental therapy for Duchenne muscular dystrophy, the biotech has closed a public offering that raised an impressive ...

The Parent Project Muscular Dystrophy (PPMD ... setback is part of the journey toward advancing therapies for Duchenne and Becker, and we draw strength from the resilience and courage of our ...

Sznajder says about 95% of children with autism have an additional symptom, and that there is a comorbidity between autism and more than 100 other diseases, including myotonic dystrophy.