The drug, discovered by Japan Tobacco and once in the hands of Merck, was licensed by BridgeBio in 2019.

A once-rare disease that causes a person to develop a severe allergy to red meat is seeing an “explosive rise” across America ...

PAP is a rare lung condition that can be difficult to diagnose because it may mimic many other more common lung diseases,” ...

Kerala state health minister Veena George said 23 patients have so far died due to amoebic encephalitis (brain fever). Kollam and Thiruvananthapuram districts are among the most affected areas, with ...

Grammy-winning R&B artist D’Angelo has died at 51 after a private battle with pancreatic cancer. His death spotlights a disease that is often diagnosed late, carries poor survival rates, and is ...

Nashville star Isabelle Tate’s death is bringing attention to a rare disease. On Thursday, October 23, news broke that the ...

New clinical-stage company will accelerate treatments for patients with ultra-rare diseases worldwide PHILADELPHIA, Oct. 7, 2025 /PRNewswire/ -- Gemma Biotherapeutics ("GEMMABio") – a leading global ...

Having already established a commercial infrastructure for its oral hereditary angioedema (HAE) drug Orladeyo and eager to pinpoint the source of its future growth, BioCryst Pharmaceuticals has struck ...

Leiden researchers have found clues to why a rare pregnancy disorder is mild in some babies but life-threatening in others.

The Calkins family is seeking a living liver donor for their toddler, Isaac, who was born with a rare disease.

Gluten allergy affects over one in ten people globally, and most people who think they have one could actually be wrong, a ...