Definition of Duchenne Muscular Dystrophy (DMD ... Three other diseases that fall into this group are: Becker muscular dystrophy or (BMD), this is a mild form of DMD Intermediate clinical ...

This year's Futures National Conference, hosted by CureDuchenne for the Duchenne and Becker MD communities, is scheduled to ...

The Parent Project Muscular Dystrophy (PPMD ... setback is part of the journey toward advancing therapies for Duchenne and Becker, and we draw strength from the resilience and courage of our ...

Newborn screening is also cost-effective. Testing that takes just a few dollars per baby can save families and the health ...

Columnist Patrick Moeschen highlights some key federal programs and pieces of legislation in the history of muscular ...

Two dose levels of a single-administration gene therapy were well-tolerated and led to functional improvements in ambulatory ...

The FDA approved Elevidys in June 2024 for young patients with Duchenne muscular dystrophy, a rare genetic condition that weakens the body’s muscles. In October, a phase 3 clinical trial found ...

Is dystrophin immunogenicity a barrier to advancing gene therapy for Duchenne muscular dystrophy? Gene Therapy , 2025; DOI: 10.1038/s41434-025-00531-y Cite This Page : ...